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Research News - Type A & B

 

Who could resist free trips to New York City while helping kids at the same time?Hello from Anne OConnor-Smith in Florida!  I would like you all to be aware that Genzyme Corporation is currently recruiting adults with Niemann-Pick Type B to participate in a single dose study of lab-created enzyme rhASM to be administered at Mt. Sinai Hospital in New York City.  This study needs 15 patients but only has 9 signed up so far and so the study is now accepting patients from the UK and Germany........Read more

Niemann-Pick Type B Latest Research News - Update from Genzyme

 

Betsy Bogard of Genzyme reports on Phase 1 Clinical study of rhASM as a potential treatment for Niemann-Pick Type B.

 

 

 

 .......to view Betsy's full report click here